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Generation Bio Announces Two Non-Viral Gene Therapy Milestone Achievements: Target Levels of Factor VIII Expression in Hemophilia A Mice and Translation of Expression from Mice to Non-Human Primates

Jan 04, 2021 - GlobeNewswire

Data confirm delivery of closed-ended DNA to the liver via novel, cell-targeted lipid nanoparticles

Well tolerated at all dose levels in mice and non-human primates Company on track to select development candidate for hemophilia A and begin IND-enabling studies this year, submit IND in 2022 Webcast and conference call to be held today at 8:00 a.m. EST CAMBRIDGE, Mass., Jan. 04, 2021 (GLOBE NEWSWIRE) --   Generation Bio Co. (Nasdaq: GBIO), an innovative genetic medicines company cre...